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BioMed Research International
Volume 2013 (2013), Article ID 402369, 8 pages
http://dx.doi.org/10.1155/2013/402369
Review Article

Development of Multiexon Skipping Antisense Oligonucleotide Therapy for Duchenne Muscular Dystrophy

1Department of Physiology, Anatomy and Genetics, University of Oxford, South Parks Road, Oxford OX1 3QX, UK
2Department of Medical Genetics, School of Human Development, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB, Canada T6G 2H7
3The Friends of Garrett Cumming Research and Muscular Dystrophy Canada HM Toupin Neurological Science Research Chair, University of Alberta, Edmonton, AB, Canada T6G 2H7

Received 30 April 2013; Accepted 18 June 2013

Academic Editor: Akinori Nakamura

Copyright © 2013 Yoshitsugu Aoki et al. This is an open access article distributed under the Creative Commons Attribution License, which permits unrestricted use, distribution, and reproduction in any medium, provided the original work is properly cited.

Citations to this Article [6 citations]

The following is the list of published articles that have cited the current article.

  • Yusuke Echigoya, and Toshifumi Yokota, “Skipping Multiple Exons of Dystrophin Transcripts Using Cocktail Antisense Oligonucleotides,” Nucleic Acid Therapeutics, pp. 131231075231009, 2013. View at Publisher · View at Google Scholar
  • Hongmei Lisa Li, Takao Nakano, and Akitsu Hotta, “Genetic correction using engineered nucleases for gene therapy applications,” Development, Growth & Differentiation, 2013. View at Publisher · View at Google Scholar
  • Stephanie A. Fernandes, Andrew G. L. Douglas, Miguel A. Varela, Matthew J. A. Wood, and Yoshitsugu Aoki, “Oligonucleotide-Based Therapy for FTD/ALS Caused by the C9orf72 Repeat Expansion: A Perspective,” Journal of Nucleic Acids, vol. 2013, pp. 1–11, 2013. View at Publisher · View at Google Scholar
  • Giulietta Riboldi, Chiara Zanetta, Michela Ranieri, Monica Nizzardo, Chiara Simone, Francesca Magri, Nereo Bresolin, Giacomo P. Comi, and Stefania Corti, “Antisense Oligonucleotide Therapy for the Treatment of C9ORF72 ALS/FTD Diseases,” Molecular Neurobiology, 2014. View at Publisher · View at Google Scholar
  • Annemieke Aartsma-Rus, Alessandra Ferlini, Nathalie Goemans, Anna M.G. Pasmooij, Dominic J. Wells, Katerine Bushby, Elizabeth Vroom, and Pavel Balabanov, “Translational and Regulatory Challenges for Exon Skipping Therapies,” Human Gene Therapy, vol. 25, no. 10, pp. 885–892, 2014. View at Publisher · View at Google Scholar
  • Marcel Veltrop, and Annemieke Aartsma-Rus, “Antisense-mediated exon skipping: Taking advantage of a trick from Mother Nature to treat rare genetic diseases,” Experimental Cell Research, 2014. View at Publisher · View at Google Scholar