Research Article
Achievement of Therapeutic Goals with Low-Dose Imiglucerase in Gaucher Disease: A Single-Center Experience
Table 1
Baseline values for surveyed parameters and after 4 years (), value between value of difference at four years from baseline, and percent of patients achieving goal for that parameter at four years (Student's -test and logistic regression with significance level of 5% were predetermined.). Therapeutic goals are as described by Pastores et al. (2004) [7] and as presented in Table 2.
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US: ultrasound; NA: not applicable. |