Review Article

Translational Research in Stem Cell Treatment of Neuromuscular Diseases

Table 5

Table summarizing the preclinical studies on the treatment of muscular dystrophies with stem cells.

Stem cellReferences

Mouse BMCs (as a vehicle for gene delivery)[34, 35]
Mouse BMCs[39, 125128]
Mouse HSCs[40]
Dog HSCs[129]
Human HSCs[130]
Human BMCs[131, 132]
Mouse MDSCs (as a vehicle for gene delivery)[36]
Mouse MDSCs[133135]
Dog MDSCs[136]
Human MDSCs[137, 138]
Mouse mesoangioblasts (as a vehicle for gene delivery)[5]
Mouse mesoangioblasts[139142]
Canine mesoangioblasts[143]
Mouse iPS[144146]
Human ASCs[147152]
Mouse myoblasts/MPCs[135, 153165]
Dog myoblast/MPCs[166]
Porcine myoblast/MPCs[167]
Monkey myoblasts/MPCs[33]
Human myoblast/MPCs[168172]
Human UCBCs[148, 173, 174]
Human SSCs*[175, 176]
Mouse ESCs[177, 178]
Mouse ESC-derived myogenic precursors[179]
Mouse BMC-derived myogenic precursors[32, 180]
Mouse satellite cells[38]
Human primordial germ cells[181]
Human IDPSC**[182]
Human primary fetal skeletal muscle cells[183]
hfMSCs***[184, 185]
BM transplantation (in mice)[186]
Mouse side population cells (as a vehicle for gene delivery)[37]

*Synovial stem cells, **human immature dental pulp stem cells, ***human fetal mesenchymal stem cells.