Advances in Hematology / 2013 / Article / Tab 3

Research Article

Achievement of Therapeutic Goals with Low-Dose Imiglucerase in Gaucher Disease: A Single-Center Experience

Table 3

Percent of patients achieving therapeutic goals in 4 years.

Therapeutic goalCurrent study ( )Change in 4 years

Anemia9.1% to 81.7% 72.6%
Thrombocytopenia20.7% to 68.9% 48.2%
Splenomegaly60.0% at 4 years ND
Hepatomegaly53.1% at 4 yearsND
No bone pain42.1% to 59.9% 17.8%
No bone crises91.5% to 93.8% 2.3%
No osteonecrosis78.7% to 92.6% 13.9%
LS Z-score 69.9% at 4 yearsND
FN Z-score 70.6% at 4 yearsND

ND: not done.

Article of the Year Award: Outstanding research contributions of 2020, as selected by our Chief Editors. Read the winning articles.