Biodistribution and Molecular Studies on Orally Administered Nanoparticle-AON Complexes Encapsulated with Alginate Aiming at Inducing Dystrophin Rescue in mdx Mice
Table 1
Nanoparticles characteristics.
Sample
Diameter (SEM) nm (±standard error of the mean)
Diameter (PCS) nm (±polydispersity index)
Quaternary ammonium groups mol/g
Primary amino groups mol/g
NIPAM
Studies
ZM2
202
—
yes
Functional analysis (dystrophin rescue) with ZM2-AON and ZM2-AON alginate